Discovery of ATP competitive PDHK1/2 dual inhibitors
- Bioorg Med Chem Lett. 2025 Jul 1:122:130190. doi: 10.1016/j.bmcl.2025.130190.
- 1. China Innovation Center of Roche, No. 371 Lishizhen Road, Shanghai, 201203, China.
- 2. Pharmaceutical Research and Early Development, F. Hoffmann-La Roche AG, Roche Innovation Center Basel, Grenzacherstrasse 124, 4070 Basel, Switzerland.
- 3. China Innovation Center of Roche, No. 371 Lishizhen Road, Shanghai, 201203, China. Electronic address: [email protected].
Multiple screening approaches were carried out to identify novel chemistry starting for Pyruvate Dehydrogenase Kinases (PDHKs) inhibitors. Through hit triaging efforts and structure-based optimization, two series of ATP competitive inhibitors with single digit nanomolar enzymatic potency for PDHK1/2 and around 10-100-fold selectivity over PDHK4/3 were discovered. Approach of covalent inhibitor was explored to successfully improve the cellular target engagement to single digit micromolar range.