1 Result for "

SRP5051

" in MedChemExpress (MCE) Product Catalog:
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1 Results for "SRP5051" in MCE Product Catalog:

Vesleteplirsen sodium
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RNA, [P-deoxy-P-(dimethylamino)](2',3'-dideoxy-2',3'-imino-2',3'-seco)(2'a→5')(C-m5U-C-C-A-A-C-A-m5U-C-A-A-G-G-A-A-G-A-m5U-G-G-C-Am5U-m5U-m5U-C-m5U-A-[2'a-(N2-acetyl-L-arginyl-L-arginyl-L-arginyl-Larginyl-L-arginyl-L-arginylglycyl)]G), 5'-[P-[4-[[2-[2-(2-hydroxyethoxy)ethoxy]ethoxy]carbonyl]-1-piperazinyl]-N,Ndimethylphosphonamidate], sodium salt
Cat. No.: HY-132585A
Synonyms: SRP-5051 sodium
Vesleteplirsen (SRP-5051) sodium is a next-generation antisense oligonucleotide of peptide phosphorodiamidate morpholino oligomer (PPMO). Vesleteplirsen targets exon 51 skipping in Duchenne muscular dystrophy (DMD) .
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