A non-viral CRISPR/Cas9 delivery system for therapeutically targeting HBV DNA and pcsk9 in vivo
- Cell Res. 2017 Mar;27(3):440-443. doi: 10.1038/cr.2017.16.
Affiliations
- 1. School of Pharmaceutical Sciences, Center for Infectious Disease Research, School of Medicine, Tsinghua University, Tsinghua-Peking Center for Life Sciences, Beijing 100084, China.
- 2. Division of Pharmaceutics and Pharmaceutical Chemistry, College of Pharmacy, The Ohio State University, Columbus, OH 43210, USA.
- 3. Department of Biomedical Engineering, School of Medicine, Tsinghua University, Beijing 100084, China.
PMID: 28117345
DOI: 10.1038/cr.2017.16