Elexacaftor/Tezacaftor/Ivacaftor Improved Clinical Outcomes in a Patient with N1303K-CFTR Based on In Vitro Experimental Evidence

  • Am J Respir Crit Care Med. 2021 Nov 15;204(10):1231-1235. doi: 10.1164/rccm.202101-0090LE.
Yunjie Huang  1 Grace Paul  2 Jesun Lee  1 Sunitha Yarlagadda  1 Karen McCoy  2 Anjaparavanda P Naren  1
Affiliations
  • 1. Cincinnati Children's Hospital Medical Center Cincinnati, Ohio.
  • 2. Nationwide Children's Hospital Columbus, Ohio.
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